Oncology and immuno-oncology
Multiple myeloma ⏐ Leukaemia ⏐Lymphomas ⏐Brain, breast, ovarian, lung, kidney, pancreatic, prostate and skin cancers
Rare and ultra-rare diseases
Haemophilia ⏐ Spinal muscular atrophy (SMA)⏐ Cystic fibrosis ⏐ Progressive familial intrahepatic cholestasis (PFIC) ⏐ Alagille syndrome (ALGS) ⏐ Primary immunodeficiency diseases ⏐ Chronic lymphocytic leukaemia